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LT2841578T - Rnr moduliuojantys oligonukleotidai su pagerintomis savybėmis, skirti neuromuskulinių susirgimų gydymui - Google Patents

Rnr moduliuojantys oligonukleotidai su pagerintomis savybėmis, skirti neuromuskulinių susirgimų gydymui

Info

Publication number
LT2841578T
LT2841578T LTEP13720617.3T LT13720617T LT2841578T LT 2841578 T LT2841578 T LT 2841578T LT 13720617 T LT13720617 T LT 13720617T LT 2841578 T LT2841578 T LT 2841578T
Authority
LT
Lithuania
Prior art keywords
treatment
improved characteristics
neuromuscular disorders
modulating oligonucleotides
rna modulating
Prior art date
Application number
LTEP13720617.3T
Other languages
English (en)
Inventor
Peter Christian De Visser
Susan Allegonda Maria MULDERS
Original Assignee
Biomarin Technologies B.V.
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Biomarin Technologies B.V. filed Critical Biomarin Technologies B.V.
Publication of LT2841578T publication Critical patent/LT2841578T/lt

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    • C12N15/00—Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor
    • C12N15/09—Recombinant DNA-technology
    • C12N15/11—DNA or RNA fragments; Modified forms thereof; Non-coding nucleic acids having a biological activity
    • C12N15/113—Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides; Antisense DNA or RNA; Triplex- forming oligonucleotides; Catalytic nucleic acids, e.g. ribozymes; Nucleic acids used in co-suppression or gene silencing
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P21/00—Drugs for disorders of the muscular or neuromuscular system
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P21/00—Drugs for disorders of the muscular or neuromuscular system
    • A61P21/02—Muscle relaxants, e.g. for tetanus or cramps
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
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    • A61P25/00—Drugs for disorders of the nervous system
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    • A61P25/00—Drugs for disorders of the nervous system
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    • A—HUMAN NECESSITIES
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    • A61P25/00—Drugs for disorders of the nervous system
    • A61P25/28—Drugs for disorders of the nervous system for treating neurodegenerative disorders of the central nervous system, e.g. nootropic agents, cognition enhancers, drugs for treating Alzheimer's disease or other forms of dementia
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  • Saccharide Compounds (AREA)
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LTEP13720617.3T 2012-04-23 2013-04-23 Rnr moduliuojantys oligonukleotidai su pagerintomis savybėmis, skirti neuromuskulinių susirgimų gydymui LT2841578T (lt)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201261636914P 2012-04-23 2012-04-23
EP12165139 2012-04-23
PCT/NL2013/050306 WO2013162363A1 (en) 2012-04-23 2013-04-23 RNA modulating oligonucleotides with improved characteristics for the treatment of neuromuscular disorders

Publications (1)

Publication Number Publication Date
LT2841578T true LT2841578T (lt) 2017-09-25

Family

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Family Applications (1)

Application Number Title Priority Date Filing Date
LTEP13720617.3T LT2841578T (lt) 2012-04-23 2013-04-23 Rnr moduliuojantys oligonukleotidai su pagerintomis savybėmis, skirti neuromuskulinių susirgimų gydymui

Country Status (19)

Country Link
US (4) US9745576B2 (lt)
EP (4) EP4400169A2 (lt)
JP (4) JP6174678B2 (lt)
CN (2) CN104271741A (lt)
AU (1) AU2013253074C1 (lt)
BR (1) BR112014026285B1 (lt)
CA (2) CA2870697C (lt)
DK (1) DK2841578T3 (lt)
ES (2) ES2983421T3 (lt)
HK (1) HK1207118A1 (lt)
HR (1) HRP20171254T1 (lt)
HU (1) HUE033431T2 (lt)
LT (1) LT2841578T (lt)
NZ (1) NZ700561A (lt)
PL (1) PL2841578T3 (lt)
PT (1) PT2841578T (lt)
RS (1) RS56319B1 (lt)
SI (1) SI2841578T1 (lt)
WO (1) WO2013162363A1 (lt)

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