ZA200701943B - Compositions and their uses for lysosomal enzyme deficiencies - Google Patents
Compositions and their uses for lysosomal enzyme deficiencies Download PDFInfo
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- ZA200701943B ZA200701943B ZA200701943A ZA200701943A ZA200701943B ZA 200701943 B ZA200701943 B ZA 200701943B ZA 200701943 A ZA200701943 A ZA 200701943A ZA 200701943 A ZA200701943 A ZA 200701943A ZA 200701943 B ZA200701943 B ZA 200701943B
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- A61K47/50—Medicinal preparations characterised by the non-active ingredients used, e.g. carriers or inert additives; Targeting or modifying agents chemically bound to the active ingredient the non-active ingredient being chemically bound to the active ingredient, e.g. polymer-drug conjugates
- A61K47/69—Medicinal preparations characterised by the non-active ingredients used, e.g. carriers or inert additives; Targeting or modifying agents chemically bound to the active ingredient the non-active ingredient being chemically bound to the active ingredient, e.g. polymer-drug conjugates the conjugate being characterised by physical or galenical forms, e.g. emulsion, particle, inclusion complex, stent or kit
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- A61K48/0008—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'non-active' part of the composition delivered, e.g. wherein such 'non-active' part is not delivered simultaneously with the 'active' part of the composition
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- A61K48/0008—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'non-active' part of the composition delivered, e.g. wherein such 'non-active' part is not delivered simultaneously with the 'active' part of the composition
- A61K48/0025—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'non-active' part of the composition delivered, e.g. wherein such 'non-active' part is not delivered simultaneously with the 'active' part of the composition wherein the non-active part clearly interacts with the delivered nucleic acid
- A61K48/0041—Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases; Gene therapy characterised by an aspect of the 'non-active' part of the composition delivered, e.g. wherein such 'non-active' part is not delivered simultaneously with the 'active' part of the composition wherein the non-active part clearly interacts with the delivered nucleic acid the non-active part being polymeric
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ZA (1) | ZA200701943B (fr) |
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US7906492B2 (en) | 2001-01-16 | 2011-03-15 | Sloan-Kettering Institute For Cancer Research | Therapy-enhancing glucan |
US7878978B2 (en) | 2004-03-18 | 2011-02-01 | University Of Pittsburgh- Of The Commonwealth System Of Higher Education | Use of relaxin to increase arterial compliance |
US7740861B2 (en) | 2004-06-16 | 2010-06-22 | University Of Massachusetts | Drug delivery product and methods |
CN101052383B (zh) | 2004-09-17 | 2013-01-30 | 马萨诸塞大学 | 用于溶酶体酶缺乏症的组合物和其用途 |
US20090209624A1 (en) * | 2005-10-24 | 2009-08-20 | University Of Massachusetts | Compositions and their uses for gene therapy of bone conditions |
IN2014DN08830A (fr) * | 2006-02-02 | 2015-07-10 | Globeimmune Inc | |
US20080044438A1 (en) * | 2006-03-17 | 2008-02-21 | Ostroff Gary R | Yeast Cell Particles As Oral Delivery Vehicles For Antigens |
US20090022799A1 (en) * | 2006-10-06 | 2009-01-22 | Shikha Pramanik Barman | Compositions that contain beta-glucan to be used for the prevention and treatment of disease and methods for their use |
US20100111985A1 (en) * | 2007-04-25 | 2010-05-06 | Orbis Health Solutions, Llc | Vaccine compositions and methods of use |
EP2222283A2 (fr) * | 2007-10-29 | 2010-09-01 | University of Massachusetts | Proteins de levure membranaire encapsulées de facon multilayer pour l'administration d'acides nucléiques (siadn) |
US8815818B2 (en) | 2008-07-18 | 2014-08-26 | Rxi Pharmaceuticals Corporation | Phagocytic cell delivery of RNAI |
WO2010078536A1 (fr) | 2009-01-05 | 2010-07-08 | Rxi Pharmaceuticals Corporation | Inhibition de pcsk9 par arni |
JP5292118B2 (ja) * | 2009-01-30 | 2013-09-18 | 富士フイルム株式会社 | 蛍光内視鏡システム及び蛍光内視鏡システムの作動方法 |
WO2012024229A1 (fr) | 2010-08-14 | 2012-02-23 | University Of Massachusetts | Particule de paroi cellulaire de levures pour administrer des nanoparticules ciblées sur le récepteur |
KR101619815B1 (ko) | 2011-04-04 | 2016-05-12 | 주식회사 메디진바이오 | 리소좀 효소를 유효성분으로 포함하는 뮤코지방증 ii의 예방 또는 치료용 약학 조성물 |
WO2013018091A1 (fr) * | 2011-08-04 | 2013-02-07 | Ramot At Tel-Aviv Universitiy Ltd. | Particules destinées au traitement de maladies neurodégénératives |
DK2865278T3 (en) * | 2012-06-25 | 2016-09-19 | S A Damm | Binder fat obtained from biomass, derived from beer production |
US9744193B2 (en) | 2012-09-06 | 2017-08-29 | Orbis Health Solutions Llc | Tumor lysate loaded particles |
AU2013359392C1 (en) | 2012-12-12 | 2016-12-08 | Orbis Health Solutions, Llc | Compositions and methods for tissue regeneration |
US10335433B2 (en) | 2013-04-10 | 2019-07-02 | Mimedx Group, Inc. | NDGA polymers and metal complexes thereof |
EP2991488A4 (fr) * | 2013-05-02 | 2016-12-21 | The Chancellor Masters And Scholars Of The Univ Of Oxford | Inhibition de glycolipides à l'aide d'iminosucres |
JP6797022B2 (ja) | 2014-03-05 | 2020-12-09 | オービス ヘルス ソリューションズ エルエルシー | 酵母細胞壁粒子を用いたワクチン送達系 |
US9981021B1 (en) | 2015-04-09 | 2018-05-29 | Kinetiq, Inc. | Subcutaneous therapeutic enzyme formulations, uses, and methods for generating thereof |
US11612619B2 (en) | 2018-11-01 | 2023-03-28 | National Institute Of Health (Nih), U.S. Dept. Of Health And Human Services (Dhhs), U.S. Government | Compostions and methods for enabling cholesterol catabolism in human cells |
CN112315944B (zh) * | 2020-12-08 | 2022-09-02 | 黄山中皇制药有限公司 | 一种穿琥宁肠溶干混悬剂的制备方法 |
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-
2005
- 2005-09-19 CN CN2005800375764A patent/CN101052383B/zh not_active Expired - Fee Related
- 2005-09-19 ES ES05814893T patent/ES2375995T3/es active Active
- 2005-09-19 AT AT05814893T patent/ATE536175T1/de active
- 2005-09-19 US US11/230,017 patent/US8007814B2/en active Active
- 2005-09-19 BR BRPI0515332-8A patent/BRPI0515332A/pt not_active IP Right Cessation
- 2005-09-19 EP EP05814893A patent/EP1802289B1/fr not_active Not-in-force
- 2005-09-19 AU AU2005284727A patent/AU2005284727A1/en not_active Abandoned
- 2005-09-19 KR KR1020077008585A patent/KR20070054246A/ko not_active Application Discontinuation
- 2005-09-19 WO PCT/US2005/033300 patent/WO2006032039A2/fr active Application Filing
- 2005-09-19 CA CA2580537A patent/CA2580537C/fr not_active Expired - Fee Related
- 2005-09-19 JP JP2007532543A patent/JP5302537B2/ja not_active Expired - Fee Related
-
2007
- 2007-03-06 ZA ZA200701943A patent/ZA200701943B/en unknown
- 2007-03-06 IL IL181748A patent/IL181748A/en active IP Right Grant
- 2007-10-10 HK HK07110965.3A patent/HK1105587A1/xx not_active IP Right Cessation
-
2011
- 2011-07-29 US US13/194,469 patent/US8637045B2/en not_active Expired - Lifetime
Also Published As
Publication number | Publication date |
---|---|
CN101052383A (zh) | 2007-10-10 |
ES2375995T3 (es) | 2012-03-08 |
JP2008513484A (ja) | 2008-05-01 |
AU2005284727A1 (en) | 2006-03-23 |
EP1802289A2 (fr) | 2007-07-04 |
JP5302537B2 (ja) | 2013-10-02 |
CN101052383B (zh) | 2013-01-30 |
KR20070054246A (ko) | 2007-05-28 |
WO2006032039A3 (fr) | 2007-04-05 |
US8007814B2 (en) | 2011-08-30 |
BRPI0515332A (pt) | 2008-07-22 |
EP1802289B1 (fr) | 2011-12-07 |
US8637045B2 (en) | 2014-01-28 |
IL181748A (en) | 2013-12-31 |
CA2580537A1 (fr) | 2006-03-23 |
US20120039929A1 (en) | 2012-02-16 |
ATE536175T1 (de) | 2011-12-15 |
IL181748A0 (en) | 2008-04-13 |
CA2580537C (fr) | 2015-04-21 |
HK1105587A1 (en) | 2008-02-22 |
WO2006032039A2 (fr) | 2006-03-23 |
US20060083718A1 (en) | 2006-04-20 |
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