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HK1245670A1 - 對抗肌肉病症的裝置和方法 - Google Patents

對抗肌肉病症的裝置和方法

Info

Publication number
HK1245670A1
HK1245670A1 HK18105446.9A HK18105446A HK1245670A1 HK 1245670 A1 HK1245670 A1 HK 1245670A1 HK 18105446 A HK18105446 A HK 18105446A HK 1245670 A1 HK1245670 A1 HK 1245670A1
Authority
HK
Hong Kong
Prior art keywords
methods
muscle disorders
counteracting muscle
counteracting
disorders
Prior art date
Application number
HK18105446.9A
Other languages
English (en)
Inventor
Johannes De Kimpe Josephus
Johannes Platenburg Gerardus
Christina Theodora Van Deutekom Judith
Aartsma-Rus Annemieke
Boudewijn Van Ommen Garrit-Jan
Original Assignee
Academisch Ziekenhuis Leiden
Biomarin Tech Bv
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Family has litigation
First worldwide family litigation filed litigation Critical https://patents.darts-ip.com/?family=39045623&utm_source=google_patent&utm_medium=platform_link&utm_campaign=public_patent_search&patent=HK1245670(A1) "Global patent litigation dataset” by Darts-ip is licensed under a Creative Commons Attribution 4.0 International License.
Application filed by Academisch Ziekenhuis Leiden, Biomarin Tech Bv filed Critical Academisch Ziekenhuis Leiden
Publication of HK1245670A1 publication Critical patent/HK1245670A1/zh

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    • A61K31/33—Heterocyclic compounds
    • A61K31/395—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
    • A61K31/495—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with two or more nitrogen atoms as the only ring heteroatoms, e.g. piperazine or tetrazines
    • A61K31/505—Pyrimidines; Hydrogenated pyrimidines, e.g. trimethoprim
    • A61K31/519—Pyrimidines; Hydrogenated pyrimidines, e.g. trimethoprim ortho- or peri-condensed with heterocyclic rings
    • A61K31/52—Purines, e.g. adenine
    • A61K31/522—Purines, e.g. adenine having oxo groups directly attached to the heterocyclic ring, e.g. hypoxanthine, guanine, acyclovir
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    • A61K31/573—Compounds containing cyclopenta[a]hydrophenanthrene ring systems; Derivatives thereof, e.g. steroids substituted in position 17 beta by a chain of two carbon atoms, e.g. pregnane or progesterone substituted in position 21, e.g. cortisone, dexamethasone, prednisone or aldosterone
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    • A61K38/16—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof
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    • A61K38/1703—Peptides having more than 20 amino acids; Gastrins; Somatostatins; Melanotropins; Derivatives thereof from animals; from humans from vertebrates
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HK18105446.9A 2007-10-26 2018-04-26 對抗肌肉病症的裝置和方法 HK1245670A1 (zh)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US67007P 2007-10-26 2007-10-26
EP07119351 2007-10-26

Publications (1)

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HK1245670A1 true HK1245670A1 (zh) 2018-08-31

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HK13112417.5A HK1185098A1 (zh) 2007-10-26 2012-01-16 高效跳過裘馨氏肌肉營養不良症前體 外顯子 的方法和工具
HK18105446.9A HK1245670A1 (zh) 2007-10-26 2018-04-26 對抗肌肉病症的裝置和方法

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Country Status (17)

Country Link
US (19) US9243245B2 (zh)
EP (4) EP3238737B1 (zh)
JP (6) JP5600064B2 (zh)
CN (5) CN101896186A (zh)
AU (1) AU2008317566B2 (zh)
CA (1) CA2704049A1 (zh)
CY (2) CY1117286T1 (zh)
DK (1) DK2203173T3 (zh)
ES (5) ES2564563T3 (zh)
HK (2) HK1185098A1 (zh)
HR (1) HRP20160025T1 (zh)
HU (2) HUE028662T2 (zh)
IL (4) IL205322A (zh)
NZ (2) NZ584793A (zh)
PL (1) PL2203173T3 (zh)
PT (1) PT2203173E (zh)
WO (1) WO2009054725A2 (zh)

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EP1191097A1 (en) * 2000-09-21 2002-03-27 Leids Universitair Medisch Centrum Induction of exon skipping in eukaryotic cells
WO2004083432A1 (en) 2003-03-21 2004-09-30 Academisch Ziekenhuis Leiden Modulation of exon recognition in pre-mrna by interfering with the secondary rna structure
PL3103800T3 (pl) 2003-04-11 2018-11-30 Ptc Therapeutics, Inc. Związki kwasu 1,2,4-oksadiazolobenzoesowego i ich zastosowanie do supresji mutacji nonsensownych i leczenia choroby
EP3808845A1 (en) 2004-06-28 2021-04-21 The University Of Western Australia Antisense oligonucleotides for inducing exon skipping and methods of use thereof
USRE48960E1 (en) 2004-06-28 2022-03-08 The University Of Western Australia Antisense oligonucleotides for inducing exon skipping and methods of use thereof
ES2852549T3 (es) 2005-02-09 2021-09-13 Sarepta Therapeutics Inc Composición antisentido para tratamiento de la atrofia muscular
CA2660523C (en) 2006-08-11 2019-03-19 Prosensa Technologies B.V. Methods and means for treating dna repeat instability associated genetic disorders
PL2203173T3 (pl) 2007-10-26 2016-06-30 Academisch Ziekenhuis Leiden Środki i sposoby przeciwdziałania zaburzeniom mięśni
EP2119783A1 (en) * 2008-05-14 2009-11-18 Prosensa Technologies B.V. Method for efficient exon (44) skipping in Duchenne Muscular Dystrophy and associated means
US8084601B2 (en) 2008-09-11 2011-12-27 Royal Holloway And Bedford New College Royal Holloway, University Of London Oligomers
TR201902952T4 (tr) 2008-10-24 2019-03-21 Sarepta Therapeutics Inc Dmd için ekson atlama bileşimleri.
AU2009310557B2 (en) * 2008-10-27 2014-09-11 Academisch Ziekenhuis Leiden Methods and means for efficient skipping of exon 45 in Duchenne Muscular Dystrophy pre-mRNA
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JP2014111638A (ja) 2014-06-19
JP2021113229A (ja) 2021-08-05
US11427820B2 (en) 2022-08-30
US20230151362A1 (en) 2023-05-18
ES2936464T3 (es) 2023-03-17
DK2203173T3 (en) 2016-02-29
AU2008317566B2 (en) 2014-05-01
HK1185098A1 (zh) 2014-02-07
US20110263682A1 (en) 2011-10-27
US10876114B2 (en) 2020-12-29
US9243245B2 (en) 2016-01-26
CN102264903B (zh) 2015-01-07
EP2614827B1 (en) 2017-06-28
CN105647921A (zh) 2016-06-08
WO2009054725A3 (en) 2009-10-15
US20200239886A1 (en) 2020-07-30
CY1117454T1 (el) 2017-04-26
US20120022134A1 (en) 2012-01-26
WO2009054725A2 (en) 2009-04-30
US20150073037A1 (en) 2015-03-12
CY1117286T1 (el) 2017-04-26
EP3238737B1 (en) 2022-04-06
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EP2203173B1 (en) 2015-12-23
PL2203173T3 (pl) 2016-06-30

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