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MY190213A - Modified factor ix, and compositions, methods and uses for gene transfer to cells, organs and tissues - Google Patents

Modified factor ix, and compositions, methods and uses for gene transfer to cells, organs and tissues

Info

Publication number
MY190213A
MY190213A MYPI2017001925A MYPI2017001925A MY190213A MY 190213 A MY190213 A MY 190213A MY PI2017001925 A MYPI2017001925 A MY PI2017001925A MY PI2017001925 A MYPI2017001925 A MY PI2017001925A MY 190213 A MY190213 A MY 190213A
Authority
MY
Malaysia
Prior art keywords
organs
tissues
cells
gene transfer
methods
Prior art date
Application number
MYPI2017001925A
Inventor
Katherine A High
Xavier Anguela
Original Assignee
Childrens Hospital Philadelphia
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Childrens Hospital Philadelphia filed Critical Childrens Hospital Philadelphia
Priority claimed from PCT/US2016/039075 external-priority patent/WO2016210170A1/en
Publication of MY190213A publication Critical patent/MY190213A/en

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  • Medicines Containing Material From Animals Or Micro-Organisms (AREA)

Abstract

The invention relates to modified Factor IX coding sequence, expression cassette, vectors such as viral (e.g., lenti- or adeno-associated viral) vectors, and gene transfer methods and uses. In particular, to target Factor IX nucleic acid to cells, tissues or organs for expression (transcription) of Factor IX. Figure 19
MYPI2017001925A 2015-06-23 2016-06-23 Modified factor ix, and compositions, methods and uses for gene transfer to cells, organs and tissues MY190213A (en)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
US201562183599P 2015-06-23 2015-06-23
PCT/US2016/039075 WO2016210170A1 (en) 2015-06-23 2016-06-23 Modified factor ix, and compositions, methods and uses for gene transfer to cells, organs and tissues

Publications (1)

Publication Number Publication Date
MY190213A true MY190213A (en) 2022-04-05

Family

ID=87760869

Family Applications (1)

Application Number Title Priority Date Filing Date
MYPI2017001925A MY190213A (en) 2015-06-23 2016-06-23 Modified factor ix, and compositions, methods and uses for gene transfer to cells, organs and tissues

Country Status (1)

Country Link
MY (1) MY190213A (en)

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