STS 1 Act 6 Gene Therapy
STS 1 Act 6 Gene Therapy
STS 1 Act 6 Gene Therapy
COLLEGE OF SCIENCE
DEPARTMENT OF ENVIRONMENTAL SCIENCE
SCHOOL YEAR 2021-2021
Gene therapy is an experimental method of treating disease by modifying the genetic material of
the patient. Gene therapy usually involves inserting a healthy copy of a faulty gene into the
patient's cells. The objective is to change the genetic code of the patient's disease-causing cell and
then restore normal conditions to that cell. Genes contain your DNA which governs much of the
structure and function of your body, from making you taller to regulating your body systems, is
contained in your genes.
Gene therapy attempts to cure sickness or increase your body's ability to fight disease by replacing
a broken gene or adding a new gene. Gene therapy has promise in the treatment of cancer, cystic
fibrosis, heart disease, diabetes, hemophilia, and AIDS, among other disorders.
Gene therapy has successfully addressed a number of inherited immunological disorders. Patients'
blood stem cells are usually extracted, and retroviruses are employed to give functional copies of
the faulty genes. Gene treatments are being researched to cure a variety of inherited blindness,
particularly degenerative forms in which patients lose their light-sensing cells over time.
3.) Are there risks associated with gene therapy? (10 pts)
The body's immune system may react to the newly introduced therapeutic vector as if it were an
intruder, just as it would to any other gene therapy. Inflammation and other hazardous
consequences can result from an immune system reaction. Gene therapy could result in an excess
of the protein being produced. Depending on the type of protein produced, the effect of this
overproduction, or over-expression, may differ. Gene therapy clinical trials are now evaluating the
impact of overproduction.